Gene therapies are emerging as promising treatments for previously untreatable genetic disorders, with adeno-associated viruses (AAVs) being the preferred vector for gene delivery. However, AAV-based gene therapies face challenges in production, including cost, complexity, and scalability. With the gene therapy market projected to grow significantly, drug developers are seeking platforms that streamline AAV production. Key factors include ensuring flexibility to accommodate different therapies, minimizing risks by understanding the entire process, and scaling production as projects progress. A well-designed AAV platform can enhance efficiency, quality, and regulatory compliance, ensuring safe delivery of therapies to patients.

byXiaojun Liu